Effective treatment of spinal muscular atrophy with antisense oligonucleotide therapy opens the door to treating other neurological disorders with this approach
International audienceNeuromuscular disorders include a wide range of diseases affecting the periphe...
Recent reports underscore the unparalleled potential of antisense-oligonucleotide (ASO)-based approa...
Duchenne muscular dystrophy (DMD) and spinal muscular atrophy (SMA) are two of the most common inher...
Effective treatment of spinal muscular atrophy with antisense oligonucleotide therapy opens the door...
AbstractAntisense oligonucleotides are synthetic single stranded strings of nucleic acids that bind ...
Antisense oligonucleotides (ASOs) were first discovered to influence RNA processing and modulate pro...
Neuromuscular disorders such as Duchenne Muscular Dystrophy and Spinal Muscular Atrophy are neurodeg...
Spinal muscular atrophy (SMA) is a devastating neuromuscular disorder characterized by loss of spina...
Antisense oligonucleotides represent a novel therapeutic platform for the discovery of medicines tha...
The introduction of genetics revolutionized the field of neurodegenerative and neuromuscular disease...
Antisense nucleic acids are single-stranded oligonucleotides that have been specially chemically mod...
The development of effective therapies for neuromuscular disorders such as Duchenne muscular dystrop...
Genetic neuromuscular diseases are caused by defective expression of nuclear or mitochondrial genes....
Spinal muscular atrophy (SMA) is an autosomal recessive neuromuscular disorder caused by mutations i...
Antisense oligonucleotides (ASOs) are disease-modifying agents affecting protein-coding and noncodin...
International audienceNeuromuscular disorders include a wide range of diseases affecting the periphe...
Recent reports underscore the unparalleled potential of antisense-oligonucleotide (ASO)-based approa...
Duchenne muscular dystrophy (DMD) and spinal muscular atrophy (SMA) are two of the most common inher...
Effective treatment of spinal muscular atrophy with antisense oligonucleotide therapy opens the door...
AbstractAntisense oligonucleotides are synthetic single stranded strings of nucleic acids that bind ...
Antisense oligonucleotides (ASOs) were first discovered to influence RNA processing and modulate pro...
Neuromuscular disorders such as Duchenne Muscular Dystrophy and Spinal Muscular Atrophy are neurodeg...
Spinal muscular atrophy (SMA) is a devastating neuromuscular disorder characterized by loss of spina...
Antisense oligonucleotides represent a novel therapeutic platform for the discovery of medicines tha...
The introduction of genetics revolutionized the field of neurodegenerative and neuromuscular disease...
Antisense nucleic acids are single-stranded oligonucleotides that have been specially chemically mod...
The development of effective therapies for neuromuscular disorders such as Duchenne muscular dystrop...
Genetic neuromuscular diseases are caused by defective expression of nuclear or mitochondrial genes....
Spinal muscular atrophy (SMA) is an autosomal recessive neuromuscular disorder caused by mutations i...
Antisense oligonucleotides (ASOs) are disease-modifying agents affecting protein-coding and noncodin...
International audienceNeuromuscular disorders include a wide range of diseases affecting the periphe...
Recent reports underscore the unparalleled potential of antisense-oligonucleotide (ASO)-based approa...
Duchenne muscular dystrophy (DMD) and spinal muscular atrophy (SMA) are two of the most common inher...
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