Add to ORKGGene therapy, in its current form, seems to be a promising treatment option for almost all ocular diseases, because the eye represents a unique target organ for gene therapy due to both structural and functional properties. Encouraging results obtained for Leber’s congenital amaurosis, a hereditary retinal disease in childhood that is otherwise destined to blindness, focused not only ophthalmologist’s but also other clinician’s interest in gene therapy. In this review, we will provide an overview of current gene therapy trials in the trials in ophthalmology
Gene therapy clinical trials with gene augmentation therapy for Leber Congenital Amaurosis have show...
In this “Perspective”, we discuss ocular gene therapy – the patient's perspective, the various strat...
Voretigene neparvovec‐rzyl was recently approved for the treatment of Leber Congenital Amaurosis, an...
It has been more than a year since ophthalmologists and scientists under Dr. Robin Ali′s team at the...
The past decade has seen major advances in gene‐based therapies, many of which show promise for tran...
Background: Gene therapy represents the therapeutic delivery of nucleic acid polymers into patient c...
Many clinical trials using gene therapy have shown significant therapeutic benefits and exceptional ...
Background: Gene therapy cannot be yet considered a far perspective, but a tangible therapeutic opti...
Gene therapy offers, for the first time, the possibility to cure diseases such as retinitis pigmento...
Gene therapy is a novel form of drug delivery that enlists the synthetic machinery of the patient&#x...
Over the last few years, huge progress has been made with regard to the understanding of molecular m...
Genetic mutations are the cause of inherited retinal dystrophies. The underlying genetic basis of th...
The eye is at the forefront of the application of gene therapy techniques to medicine. In the United...
The eye is at the forefront of the application of gene therapy techniques to medicine. In the United...
The eye is at the forefront of the application of gene therapy techniques to medicine. In the United...
Gene therapy clinical trials with gene augmentation therapy for Leber Congenital Amaurosis have show...
In this “Perspective”, we discuss ocular gene therapy – the patient's perspective, the various strat...
Voretigene neparvovec‐rzyl was recently approved for the treatment of Leber Congenital Amaurosis, an...
It has been more than a year since ophthalmologists and scientists under Dr. Robin Ali′s team at the...
The past decade has seen major advances in gene‐based therapies, many of which show promise for tran...
Background: Gene therapy represents the therapeutic delivery of nucleic acid polymers into patient c...
Many clinical trials using gene therapy have shown significant therapeutic benefits and exceptional ...
Background: Gene therapy cannot be yet considered a far perspective, but a tangible therapeutic opti...
Gene therapy offers, for the first time, the possibility to cure diseases such as retinitis pigmento...
Gene therapy is a novel form of drug delivery that enlists the synthetic machinery of the patient&#x...
Over the last few years, huge progress has been made with regard to the understanding of molecular m...
Genetic mutations are the cause of inherited retinal dystrophies. The underlying genetic basis of th...
The eye is at the forefront of the application of gene therapy techniques to medicine. In the United...
The eye is at the forefront of the application of gene therapy techniques to medicine. In the United...
The eye is at the forefront of the application of gene therapy techniques to medicine. In the United...
Gene therapy clinical trials with gene augmentation therapy for Leber Congenital Amaurosis have show...
In this “Perspective”, we discuss ocular gene therapy – the patient's perspective, the various strat...
Voretigene neparvovec‐rzyl was recently approved for the treatment of Leber Congenital Amaurosis, an...